Girl, 6, has sight restored through gene therapy

• Luxturna gene therapy has restored vision in a 6-year-old patient with inherited retinal dystrophy, representing a significant clinical advance in treating previously untreatable genetic eye disease
• Gene therapy delivery via subretinal injection can produce dramatic functional improvements in childhood vision loss, offering hope for early intervention before irreversible damage occurs
• Great Ormond Street's successful case demonstrates the real-world clinical impact of gene therapies now available on NHS, warranting consideration for eligible paediatric patients with inherited retinal conditions

Saffie's mum says Luxturna therapy at Great Ormond Street has been like "someone waved a magic wand".

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