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Clinical Trial ● Currently Recruiting Phase I / Phase II NCT05419492

A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome

A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome — Recruiting • Phase I / Phase II •…

📅 26 May 2026 ⏱ 1 min read
Currently Recruiting
This trial is actively seeking participants in the UK. Discuss eligibility with your patient before referring.
Status
Currently Recruiting
Phase
Phase I / Phase II
NCT ID
NCT05419492
Start
2024-05-14
Completion
2028-01
ClinicaliQ Trial Snapshot
  • A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome — Recruiting • Phase I / Phase II • NCT05419492.
  • ETX101 gene therapy trial testing safety and effectiveness in infants and children with Dravet syndrome.

Verify eligibility, endpoints and current status on the original ClinicalTrials.gov registry before acting on this summary.

Use This Page For
  • Quick orientation before opening the registry record.
  • Checking recruitment status, phase and sponsor at a glance.
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What This Trial Is Studying

ENDEAVOR is a Phase 1/2, 2-part, multicenter study to evaluate the safety and efficacy of ETX101 in participants with SCN1A-positive Dravet syndrome aged ≥6 to

Full Trial Details
View this trial on the source registry
Eligibility criteria, protocol, and results when available
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