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Clinical Trial ● Currently Recruiting Phase III NCT05744921

A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works

A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works…

📅 17 Sep 2026 ⏱ 1 min read
Currently Recruiting
This trial is actively seeking participants in the UK. Discuss eligibility with your patient before referring.
Status
Currently Recruiting
Phase
Phase III
NCT ID
NCT05744921
Start
2023-03-07
Completion
2028-10-10
ClinicaliQ Trial Snapshot
  • A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works — Recruiting • Phase III • NCT05744921.
  • Long-term safety and effectiveness of pozelimab and cemdisiran combination treatment in adults with paroxysmal nocturnal haemoglobinuria.

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  • Quick orientation before opening the registry record.
  • Checking recruitment status, phase and sponsor at a glance.
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What This Trial Is Studying

This study is researching an experimental treatment combination with two experimental drugs called pozelimab and cemdisiran. The study is focused on people with paroxysmal nocturnal hemoglobinuria (PNH). The aim of this study is to see how safe and effective the pozelimab + cemdisiran combination is for people with PNH in the long term. The pozelimab + cemdisiran combination may be referred to as "study drugs" in this section. This study is looking at several other research questions, including: * How effective is the pozelimab + cemdisiran combination? * What side…

Full Trial Details
View this trial on the source registry
Eligibility criteria, protocol, and results when available
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