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Clinical Trial ● Currently Recruiting Phase II NCT06285643

A Study of AAV2-GDNF in Adults With Moderate Parkinson’s Disease (REGENERATE-PD)

A Study of AAV2-GDNF in Adults With Moderate Parkinson’s Disease (REGENERATE-PD) — Recruiting • Phase II • Neurology • NCT06285643.

📅 29 Jun 2026 ⏱ 2 min read
Currently Recruiting
This trial is actively seeking participants in the UK. Discuss eligibility with your patient before referring.
Status
Currently Recruiting
Phase
Phase II
NCT ID
NCT06285643
Sponsor
AskBio Inc
Start
2024-06-11
ClinicaliQ Trial Snapshot
  • A Study of AAV2-GDNF in Adults With Moderate Parkinson’s Disease (REGENERATE-PD) — Recruiting • Phase II • Neurology • NCT06285643.
  • What is being tested: AAV2-GDNF is a gene therapy delivered surgically to the putamen (a key brain region affected in Parkinson's Disease) to potentially restore dopamine-producing nerve function through glial cell line-derived neurotrophic factor expression.
  • Patient eligibility overview: Adults with moderate Parkinson's Disease are enrolled in this randomized, double-blinded Phase 2 trial, with surgical delivery requiring careful patient selection based on disease stage and ability to tolerate neurosurgical intervention.
Use This Page For
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  • Checking recruitment status, phase and sponsor at a glance.
  • Connecting this trial to nearby guidelines, Drug Science and education.
What This Trial Is Studying

The objective of this randomized, surgically controlled, double-blinded, Phase 2 study is to evaluate the safety and efficacy of AAV2-GDNF delivered to the putamen in subjects with moderate Parkinson's Disease.

Eligibility Snapshot
  • : Age 1. Male and female adults 45-75 years of age inclusive, at the time of signing of informed consent Type of Subject and Disease Characteristics 2. Diagnosed with Parkinson's disease in the past 4-10 years (inclusive) as defined by the following: 1. Presence of bradykinesia PLUS any of the following: * Rigidity * Rest tremor * Postural instability 2. Presence of motor fluctuations as measured by the PD Motor Diary 3. Stable anti-parkinsonian medication regimen for >/= 4 weeks prior to screening 4. Must demonstrate responsiveness to levodopa therapy

Use the source registry for the full inclusion and exclusion criteria before discussing referral or enrolment.

Full Trial Details
View this trial on the source registry
Eligibility criteria, protocol, and results when available
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