ClinicaliQ Trial Snapshot
- A Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Subcutaneous Emicizumab in Participants From Birth to 12 Months of Age With Hemophilia A Without Inhibitors — Active Not Recruiting • Phase III • NCT04431726.
- Emicizumab injections prevent bleeding in babies under 12 months with severe haemophilia A, with safety and effectiveness monitored over 8 years.
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What This Trial Is Studying
This is a Phase IIIb, multicenter, open-label, single-arm study of prophylactic emicizumab in previously untreated and minimally treated patients at study enrollment from birth to ≤12 months of age with severe hemophilia A (intrinsic factor VIII [FVIII] level