- ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis — Recruiting • Phase III • Rare Diseases • NCT05878860.
- Gene therapy for inherited eye disease causing vision loss in males, testing safety and effectiveness in children and adults.
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This study will evaluate the safety and efficacy of ATSN-201 in subjects ≥ 5 years of age with RS1-associated X-linked retinoschisis (XLRS). Conditions: X-linked Retinoschisis Interventions: ATSN-201 Lead Sponsor: Atsena Therapeutics Inc. Planned Enrollment: 97 participants