- A Clinical Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 — Recruiting • Phase II • NCT06667453.
- This trial tests whether a new medicine (PGN-EDODM1) is safe and works for people with myotonic dystrophy type 1.
Verify eligibility, endpoints and current status on the original ClinicalTrials.gov registry before acting on this summary.
- Quick orientation before opening the registry record.
- Checking recruitment status, phase and sponsor at a glance.
- Connecting this trial to nearby guidelines, Drug Science and education.
The purpose of this study is to learn about the effects of an investigational medicine, PGN-EDODM1, to see how safe and tolerable multiple administrations of PGN-EDODM1 are for people with myotonic dystrophy type 1 (DM1) compared to placebo. Conditions: Myotonic Dystrophy 1 Interventions: PGN-EDODM1, Placebo Lead Sponsor: PepGen Inc Planned Enrollment: 24 participants