ClinicaliQ Trial Snapshot
- A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy — Active Not Recruiting • Phase II • NCT03771898.
- Spinal fluid injections of SHP611 tested to slow movement decline in children with metachromatic leukodystrophy.
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What This Trial Is Studying
The main aim of the study is to determine if SHP611 given by injection into the spinal fluid that surrounds the brain and spinal cord (intrathecal; IT) prolongs the time for children with Metachromatic Leukodystrophy (MLD) to retain the ability to move from place to place. Other aims of the study are to determine the effects of intrathecal administration of SHP611 on movement and speech functions and to learn how well SHP611 injected in the spinal fluid that surrounds the brain and spinal cord is tolerated. Study participants will receive…