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Clinical Trial Active — Not Recruiting Phase III NCT04794101

Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene

Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene — Active Not Recruiting • Phase III • Rare Diseases…

📅 08 May 2026 ⏱ 1 min read
Active — Not Recruiting
Check the registry for current status and eligibility criteria.
Status
Active — Not Recruiting
Phase
Phase III
NCT ID
NCT04794101
Start
2020-12-04
Completion
2029-09-20
ClinicaliQ Trial Snapshot
  • Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene — Active Not Recruiting • Phase III • Rare Diseases • NCT04794101.
  • Gene therapy injection into the eye shows promise for treating inherited blindness caused by RPGR gene faults in men.

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What This Trial Is Studying

A clinical trial of AAV5-hRKp.RPGR vector for participants with X-linked retinitis pigmentosa (XLRP) Conditions: X-Linked Retinitis Pigmentosa Interventions: Genetic: AAV5-hRKp.RPGR Intermediate Dose, Genetic: AAV5-hRKp.RPGR Low Dose Lead Sponsor: Janssen Research & Development, LLC Planned Enrollment: 97 participants

Full Trial Details
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Eligibility criteria, protocol, and results when available
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